Researchers at the Eye Genetics Research Unit at Children’s Medical Research Institute (CMRI) are the first in the world to use stem cells to study one of the genetic causes of Leber Congenital Amaurosis (LCA)—a rare condition that causes severe vision loss in babies and young children. Their findings suggest that gene therapy could soon help prevent blindness in affected kids.
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Scientists use stem cells to model rare genetic blindness in children
November 20, 2025
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